Oxford-based SynaptixBio, which is developing a therapy for a rare, deadly, and currently incurable rare disease (H-ABC), says it has identified the drug it will take forward into clinical trials.The ...

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Biogen is also a leading company in the oligonucleotide synthesis market. The recent FDA accelerated approval of QALSODY ...

AMX0114 is an investigational antisense oligonucleotide targeting calpain-2, a calcium-activated protease believed to play a role in ALS disease progression. The Food and Drug Administration (FDA ...

Investigators recently reopened the case. They say DNA evidence on several untested items led them to the Birnbaums. Anyone with information about this incident or any other crime is encouraged to ...

This work adds to a growing body of research examining how small Neanderthal DNA segments may continue to shape modern biology. Previous studies have explored Neanderthal gene influences on immune ...

Recent research in mice has shown that the DNA deletion in 22q11.2 deletion syndrome disrupts ... then tested if gene-targeting tools called antisense oligonucleotides (ASOs) could be used to treat ...

Spearheaded by the international Leonardo DNA Project and chronicled in a new book, Genìa Da Vinci: Genealogy and Genetics for Leonardo’s DNA, researchers are reconstructing Leonardo’s ...