Wilson's new company, Philadelphia-based Gemma Biotherapeutics, plans to start testing gene therapies in Brazil this year.

COIMBATORE: The state health department with the support of National Health Mission (NHM) is preparing to launch Centers of ...

Scientists have used personalised gene-editing therapy to successfully treat a baby with a rare genetic condition. Could this ...

Ocugen ( NASDAQ: OCGN) disclosed on Tuesday that its gene therapy candidate, OCU410ST, has been granted rare pediatric ...

The test applies to potentially thousands of different diseases, and it can even detect new ones by providing the evidence ...

Helen Born, a soon-to-be 4-year-old from Victoria, was diagnosed with Batten disease, a rare genetic disorder, earlier this ...

Many adults, like Moss, have struggled with issues they couldn't explain throughout their entire lives — until their children ...

Niemann-Pick Type C, or NPC is a relentlessly progressive and fatal genetic disorder that impacts both the body and the brain ...

Bone marrow transplants, while commonly known for treating cancers like leukemia and lymphoma, are also surprisingly used to treat various other conditions, including some genetic and autoimmune ...

Rocket Pharmaceuticals, Inc. , a fully integrated, late-stage biotechnology company advancing an integrated pipeline of genetic therapies for rare diseases, today announced an update related to ...

Doctors Rewrite DNA of Infant with Rare Genetic Disorder | Vantage with Palki Sharma In a medical first, U.S. doctors have saved an infant’s life by rewriting his DNA to fix a deadly genetic disorder ...

The FDA granted rare pediatric disease designation for OCU410ST, a gene therapy designed to treat ABCA4-associated ...