Adrian R. Krainer has been awarded the 2025 Heinrich Wieland Prize for his pioneering RNA research that led to the ...

Helping to design future anticancer drugs Study lead Professor Vlad Pena, Team Leader in the Mechanisms and Regulation of Pre-mRNA Splicing Team at the ICR said: “We revealed the first 3D structure of ...

Vigeneron GmbH has received IND approval from the FDA for VG-801, a novel mRNA trans-splicing gene therapy to treat Stargardt disease and other retinal dystrophies associated with mutations in the ...

VG801 is a novel mRNA trans-splicing gene therapy using dual adeno-associated virus (AAV) vectors to deliver the full-length human native ABCA4 gene. By targeting the genetic root cause through gene ...