Those who already own the stock may retain it for some time to see if VRTX's CF sales continue to rise and how the Casgevy ...
Vertex Pharmaceuticals (Nasdaq: VRTX) announced today a reimbursement agreement with NHS England for eligible sickle cell ...
particularly as the UK has a relatively high incidence of CF, and the second largest disease population in the world. It is two and a half years since Vertex’s Orkambi (lumacaftor+ivacaftor ...
Vertex and CRISPR reckon there are around 2,000 patients in the UK eligible for Casgevy. “Both sickle cell disease and beta thalassemia are painful, life-long conditions that in some cases can ...
Around 1,700 people could be eligible for the one-time treatment, which is seen as a less risky alternative to a donor stem ...
Vertex added it has also completed regulatory submissions for the vanzacaftor triple therapy in the EU, UK, and Canada, among ...
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UK health system to offer cutting-edge gene therapy for sickle cell disease Future of Healthcategory· January 31, 2025 The U.S. Food and Drug Administration has approved Vertex Pharmaceuticals ...