Additionally, our UCD clinical candidate is well tolerated, and we are preparing to evaluate CMP-CPS-001 in OTC heterozygotes, a population with reduced urea cycle function.

Urea cycle disorders (UCDs) constitute a group of rare, inherited metabolic conditions arising from deficiencies in key enzymes of the urea cycle – the biochemical pathway responsible for ...

Additionally, our UCD clinical candidate is well tolerated, and we are preparing to evaluate CMP-CPS-001 in OTC heterozygotes, a population with reduced urea cycle function.

In addition, comprehensive reviews and foundational studies continue to elucidate the biochemical and molecular aspects of the urea cycle, providing crucial insights that inform both current ...

In this editorial, the authors describe the foundations of an N-of-1 gene-editing study to treat an infant with a urea-cycle disorder. Department of Chemistry and Biochemistry, University of ...

Global Urea Cycle Disorder Treatment Market to Reach USD 771.0 Million by 2035, Expanding at a CAGR of 3.5% - Transparency Market Research, Inc. The global industry was valued at US$ 527.5 Mn in 2024 ...