Salk Institute scientists are looking for a new treatment strategy in microproteins, an understudied class of molecules found ...

Scientists in Japan have used CRISPR gene-editing technology to remove the extra chromosome that causes Down syndrome.

The FDA's approval of the first CRISPR-Cas9–based gene therapy marked a major milestone in biomedicine, validating genome ...

Apple snails can regrow their entire eyes. Scientists are now using them to uncover new ways to restore human vision.

Researchers at Fred Hutch Cancer Center invented a new screening method called ReLiC that uses CRISPR-Cas9 to test all the ...

CASGEVY® momentum building; >75 authorized treatment centers (ATCs) activated globally, achieving the target goal and ~115 ...

Challenges persist despite promising advance In January 2025, the National Institute for Health and Care Excellence (NICE) approved the use of the gene editing therapy exagamglogene autotemcel ...

The CRISPR-Cas9 system – a recently discovered system with bacterial origins – has the potential to overcome many of the limitations of currently available gene-silencing techniques. Earlier this year ...

Cas9 in germline editing presents opportunities for genetic disease correction, alongside risks of off-target effects and ...

Ovarian aging, characterized by diminishing egg reserves and quality, affects millions of women worldwide, often leading to infertility.

CRISPR-SCD Go to source) at UCSF Benioff Children's Hospital Oakland aims to cure sickle cell disease using non-viral CRISPR-Cas9 gene editing, a first-of-its-kind approach in the U.S.