Beta thalassemia is a blood disorder that affects the production of hemoglobin. Hemoglobin is the iron-rich protein in your red blood cells that carries oxygen throughout your body. With beta ...

Researchers have found a promising new method for gene therapy. They successfully restarted inactive genes by bringing them ...

Thus, further study is needed to define the role of iron overload in the cognitive impairment of patients with beta ... for the pathogenesis of brain injury in patients with β-thalassemia and ...

A one-time CRISPR-based gene therapy developed by Vertex Pharmaceuticals and CRISPR Therapeutics now has an additional FDA approval as a treatment for the rare blood disease beta thalassemia.

Depending on which chain is affected, it is classified as: Alpha-thalassemia: Caused by mutations in one or more of the four genes responsible for making alpha chains. Beta-thalassemia ...

People with alpha thalassemia have a change to the gene that makes the alpha globin protein. A child inherits two of these genes from each parent. Beta thalassemia: People with beta thalassemia ...

The groundbreaking treatment can now also be used to treat transfusion-dependent beta thalassemia in people 12 and older. Like sickle cell, beta thalassemia is an inherited blood disorder.

You most likely have beta thalassemia minor (one normal gene and one that causes low beta-cell-chain production), which consists of mild anemia and very small cells. This condition can look very ...

According to this study, more than half of children with the beta (β)-thalassemia trait and iron deficiency had hemoglobin A2 (HbA2) levels in the diagnostic range, supporting the potential of ...

Exagamglogene autotemcel (exa-cel) (Casgevy®) is a gene therapy for treating sickle cell disease in patients 12 years and older with recurrent vaso-occlusive crises and transfustion-dependent beta ...

Beta thalassemia is a treatable blood disorder that’s inherited, or passed down through your genes. With beta thalassemia, your body doesn’t make enough hemoglobin, which is an important ...

If you have beta thalassemia and you're pregnant -- or plan to start a family -- there are steps you should take to protect your health and you baby's health. With the right care, you should be ...